Like any new drug, gene and cell therapeutics must undergo both safety studies and a product development phase before they can be used in humans for the first time. The preclinical safety studies…
This lecture describes how adeno associated virus (AAVs) are used as vectors to transport genetic material into cells in an in-vivo gene therapy. It starts by giving a general introduction to gene…
The first part of this lecture describes the design and operation of a production facility for adeno associated viral vectors used for in-vivo gene therapy. The second part will provide an…
Advanced Therapy Medicinal Products (ATMPs) are a specialized category of medicinal products for human use that are based on genes, tissues or cells and offer groundbreaking new opportunities for the…
This lecture will give an overview on the rapidly evolving field of Gene and Cell Therapies (GCT) with its challenges for manufacturer and opportunities for patients.
In this lecture, life science entrepreneur and investor Marius Rosenberg shares his experience of commercializing life science innovation via the creation of one’s own startup.
This lecture highlights current ethical debates in stem cell research, including the use of human embryonic stem cells for research, perspective of cloning animals or humans, human germ line editing,…